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      • US FDA Orphan Drug Designation
      • Unproven (Off-Label) Treatments
      • Open Label Extension
      • Expanded Access
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      • Global Clinic Locator
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      • Genetic Roundtable Resources
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      • Nursing and Symptom Management
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      • Occupational Therapy and Activities of Daily Living
      • Physiotherapy and Mobility
      • Respiratory Care
      • Speech Therapy and Communication
      • Support for Family & Caregivers
      • Technology
    • Approved Drugs
      • Nuedexta
      • Radicava/Edaravone
      • Riluzole/Tiglutik
      • Rozebalamin/Methylcobalamin
      • Tofersen/Qalsody
    • Drugs in Development
      • AB Science – Masitinib
      • Neuronata-R/Lenzumestrocel
      • Neuvivo – NP001
      • Prilenia Therapeutics – Pridopidine
      • Ulefnersen – Ionis Pharmaceuticals
      • BrainStorm Cell Therapeutics – NurOwn
      • Clene Nanomedicine – CNM-Au8
      • Kadimastem – AstroRx
      • ILB – Tikomed
      • Methylcobalamin
      • Oral Edaravone
      • NeuroSense – PrimeC
      • SOD1 Therapies & Trials
      • T Regulatory Cell Therapies
    • Drugs No Longer in Development
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Recent Posts:

    Primary Sidebar

    • Lombana, Spain

      Lombana, Spain

    • Erwin Coppejans, Diagnosed 2007 , ALS Liga België, Belgium

      Erwin Coppejans, Diagnosed 2007 , ALS Liga België, Belgium

    • Steven Gallagher, Canada

      Steven Gallagher, Canada

    • Calum Ferguson, Diagnosed 2010 , MND Scotland, UK

      Calum Ferguson, Diagnosed 2010 , MND Scotland, UK

    • Imelda Arenas, ACELA, Colombia

      Imelda Arenas, ACELA, Colombia

    • Norm MacIsaac,  ALS Society of Canada,  ALS Society of Quebec,  Diagnosed 2014

      Norm MacIsaac, ALS Society of Canada, ALS Society of Quebec, Diagnosed 2014

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      727747090571358167

    • Wiebke Braach, Deutsche Gesellschaft für Muskelkranke, Germany

      Wiebke Braach, Deutsche Gesellschaft für Muskelkranke, Germany

    • Sharon Corosanite, Diagnosed 2014 , ALS Hope Foundation, USA

      Sharon Corosanite, Diagnosed 2014 , ALS Hope Foundation, USA

    • Ali Var, Turkey

      Ali Var, Turkey

    • Emilienne Verhaegen, ALS Liga Belgium, Diagnosed 2014

      Emilienne Verhaegen, ALS Liga Belgium, Diagnosed 2014

    • Marcel R. Wernard, Diagnosed 2016,  ALS Patients Connected,  The Netherlands

      Marcel R. Wernard, Diagnosed 2016, ALS Patients Connected, The Netherlands

    • Steve Lufkin, USA

      Steve Lufkin, USA
      IMG_3993

    • Soledad Rodriguez, FUNDELA, Diagnosed 2013, Spain

      Soledad Rodriguez, FUNDELA, Diagnosed 2013, Spain

    • Hollister

      Hollister
      hollister

    • unnamed

      unnamed

    • Oliver Juenke, Germany

      Oliver Juenke, Germany

    • Natalya Rybakova, Russia

      Natalya Rybakova, Russia

    • Jon Newsome, USA

      Jon Newsome, USA

    • Angela Jansen, Deutsche Gesellschaft für Muskelkranke e.V.-DGM, Diagnosed 1995, Germany

      Angela Jansen, Deutsche Gesellschaft für Muskelkranke e.V.-DGM, Diagnosed 1995, Germany

    • Eddy LeFrançois, Diagnosed 1992,  ALS Canada

      Eddy LeFrançois, Diagnosed 1992, ALS Canada

    • Maria Lucia Wood Saldanha, Associação Pró-Cura da ELA, Brazil

      Maria Lucia Wood Saldanha, Associação Pró-Cura da ELA, Brazil

    • Shera Mukherjee, Diagnosed 2013,  Asha Ek Hope Foundation, India

      Shera Mukherjee, Diagnosed 2013, Asha Ek Hope Foundation, India

    • Ada Garrido Benavidez, Diagnosed 2016,  FYADENMAC, Mexico

      Ada Garrido Benavidez, Diagnosed 2016, FYADENMAC, Mexico

    • Joyce Rusinak, Forbes Norris ALS Center, USA

      Joyce Rusinak, Forbes Norris ALS Center, USA

    • Valdomiro Xavier Honório, Brazil

      Valdomiro Xavier Honório, Brazil

    • Hanne Stenmose, Muskelsvindfonden, Denmark

      Hanne Stenmose, Muskelsvindfonden, Denmark

    • Steven Spencer, Diagnosed 2014 , MND New Zealand

      Steven Spencer, Diagnosed 2014 , MND New Zealand

    • Tison, USA

      Tison, USA

    • Mauril Belanger

      Mauril Belanger

    • João Marcos Andrietta, Diagnosed 2008 , ABrELA, Brazil

      João Marcos Andrietta, Diagnosed 2008 , ABrELA, Brazil

    • Daniel Hare

      Daniel Hare

    • Chen Chun-Chin

      Chen Chun-Chin

    • Len Johnrose,  MND Association,  Diagnosed 2017,  England

      Len Johnrose, MND Association, Diagnosed 2017, England

    • Phil Rossall, MND-Association, UK

      Phil Rossall, MND-Association, UK

    • Steve Gallagher, ALS Society of Canada

      Steve Gallagher, ALS Society of Canada
      Picture1

    • Amparo Muriel Engativa, Colombia

      Amparo Muriel Engativa, Colombia

    • Verónica Isabel Castro Molina, Diagnosed 2014, Argentina

      Verónica Isabel Castro Molina, Diagnosed 2014, Argentina

    • Angie Bordaen, Diagnosed 2014,  ALS Liga België, Belgium

      Angie Bordaen, Diagnosed 2014, ALS Liga België, Belgium

    • Ian and Teresa Roberts

      Ian and Teresa Roberts

    • John Dinon, MND Australia

      John Dinon, MND Australia

    • Susan Anderson, Diagnosed 2014 , Hope Loves Company,  USA

      Susan Anderson, Diagnosed 2014 , Hope Loves Company, USA

    • Carlos Alberto Báez Murillo, ACELA, Colombia

      Carlos Alberto Báez Murillo, ACELA, Colombia

    • Alberto Baez Murillo, Colombia

      Alberto Baez Murillo, Colombia

    • Michael Lee, Australia

      Michael Lee, Australia

    • Carlos Gomez Matallanas, Diagnosed 2014 , FUNDELA, Spain

      Carlos Gomez Matallanas, Diagnosed 2014 , FUNDELA, Spain

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      Maurice Leclerc, Canada

    • IMG_1211

      IMG_1211

    • Margarita Pizarro, Asociacion ELA Argentina, Diagnosed 2017, Argentina

      Margarita Pizarro, Asociacion ELA Argentina, Diagnosed 2017, Argentina

    • Roy

      Roy
      roy

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